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Allogeneic hematopoietic cell transplantation remains the single most powerful weapon in the fight against higher-risk acute myeloid leukemia, a cancer of the blood and bone marrow that can progress with terrifying speed. Now, one of the most comprehensive national analyses ever assembled has traced how the outcomes of this demanding procedure have evolved across nearly […]

Researchers trained an AI model to learn chemical patterns associated with stability in drug-like molecules and accurately predict where their hydrogen atoms should be positioned. The post Tautomer-Predictor AI Tool Identifies Stable Molecules for Drug Discovery appeared first on GEN - Genetic Engineering and Biotechnology News.

Sejong University researchers have developed a high-quality soybean with improved oxidative stability, reduced saturated fat and increased seed fatty acid content. The research team led by Hyun Uk Kim, a professor in the Department of Bio-Industrial Resources Engineering at Sejong University, created the soybean line containing up to 90.2% oleic acid using CRISPR/Cas9 gene-editing technology. The study is published in the Plant Biotechnology Journal.

Marina Temkin / TechCrunch: Colorado-based Enveda, which uses AI to discover new drugs in the natural world, raised a $311M Series E at a $2B valuation, double its valuation a year ago  —  Enveda, a biotech startup that uses AI to discover new drugs in the natural world, has raised a $311 million Series E at a $2 billion valuation.

Cancer medicine is saving more lives than ever, but the treatments themselves are quietly taking a toll on one of the body’s most vulnerable organs. A sweeping new review published in Holistic Integrative Oncology maps the growing problem of anticancer therapy-related renal injury, or ATRI, and examines whether cell-based and cell-derived therapies could finally give […]

Breast cancer is not one disease. Under the microscope, tumors may look similar, but at the molecular level they split into distinct subtypes that respond differently to treatment and carry very different prognoses. Clinicians have long relied on a 50-gene signature known as PAM50 to sort breast tumors into categories such as Luminal A, Luminal […]

Компания Anthropic заявила, что её ИИ Claude «самостоятельно обнаружил» новую ферментную систему, схожую с механизмом, лежащим в основе мощного инструмента редактирования генов CRISPR. Об этом пишет The Verge. Источник изображения: Anthropic

Компания Anthropic объявила о первом открытии, сделанном в её недавно запущенной лаборатории: модель Claude автономно обнаружила в генетических данных новую ферментную систему, напоминающую механизм редактирования генов CRISPR. Участие людей в процессе ограничилось постановкой задачи и проверкой результата.

Anthropic says Claude has found a previously undescribed enzyme system in the DNA of bacteriophages, the viruses that infect bacteria. Next to the enzyme’s gene sits a long run of repeating DNA that resembles a CRISPR array. The company does not yet know what the system does. Anthropic announced the result on Wednesday in a […] This story continues at The Next Web

The round valued the AI biotech at $2 billion. It is currently testing drugs that treat skin conditions and preserve weight loss after stopping GLP-1s.

Robert Hart / The Verge: Anthropic says Claude autonomously discovered a new enzyme system in the DNA of bacteriophages, somewhat similar to CRISPR, the first result from its new biolab  —  It took nearly 1,000 Claude agents 21 hours and 210 million tokens to uncover the ‘novel enzyme system.’

The cGAS protein is a sensor for mislocalized DNA in the cell cytoplasm, and responds by triggering STING, a regulator of the inflammatory response to damage and dysfunction. The cGAS-STING interaction produces some fraction of the maladaptive chronic inflammation characteristic of aging, as, among other reasons, mitochondrial dysfunction tends to spill mitochondrial DNA fragments into the cell cytoplasm. Nothing in the cell has only one purpose, however, and cGAS is also involved in the regulation of the DNA damage response in the cell nucleus. It is known to inhibit homologous recombination of double strand breaks, for example. An examination of cGAS in different species suggests that different variants can aid or hinder late life health via their actions in either the DNA repair context or […]

OXFORD, England — The world's first therapy designed to fix a patient's unique genetic mutation cost $1.65 million to make, a key facilitator of the project revealed Wednesday at a rare disease conference in the UK. ...

Years before bladder cancer is diagnosed, faint warning signs may already be accumulating across a patient’s medical history. Bladder cancer causes about 220,000 deaths worldwide each year, but finding it early remains difficult. Blood in the urine is its best-known warning sign, yet the same symptom can result from kidney stones, prostate problems, and other [...]

A blood stem cell molecule revealed how some childhood brain tumor mutations disrupt CoREST and led researchers to existing drugs worth testing further. A molecule used to help blood stem cells multiply has led researchers to an unexpected connection with childhood brain cancer. Scientists at Lund University found that the molecule produces a cellular effect [...]

A New York transplant surgeon’s experience waiting for a heart transplant laid bare the challenges of a system he had spent decades trying to fix.

China supplies over 90% of the technology fueling Vladimir Putin's war machine while buying billions in Russian oil under new U.S. sanctions scrutiny.

According to Basecamp, EDEN offers the ability to design long and complex DNA sequences with large serine recombinases capable of delivering those sequences precisely. The post Anthropic-, Nvidia-Backed Basecamp Research Raise $140M Series C Financing Toward Advancing AI-Designed Drugs appeared first on GEN - Genetic Engineering and Biotechnology News.

Chronic respiratory diseases such as asthma and chronic obstructive pulmonary disease, or COPD, remain among the world’s most persistent killers. In the European region alone, they account for nearly 400,000 deaths every year, with COPD responsible for roughly 80 percent of that toll, and globally respiratory illnesses rank as the third leading cause of death. […]

Generative artificial intelligence has become remarkably good at dreaming up molecules. Feed a model a protein pocket or a desired property profile, and it will happily pour out thousands of candidate structures that look, on a screen, like the next blockbuster drug. There is a catch that has haunted computational chemistry for years: a large […]

New York University researchers have trained an AI model to learn chemical patterns associated with stability in drug-like molecules and accurately predict where their hydrogen atoms should be positioned.

The Abigail Wexner Research Institute at Nationwide Children's Hospital celebrated the Food and Drug Administration's (FDA) approval of FAYUVI for Sanfilippo syndrome type A, following years of research in its Jerry R. Mendell Center for Gene Therapy to help patients with devastating diseases.

Dozens of trans activists protested outside NYU Langone and took hormone replacement therapy after the hospital agreed to end gender-affirming treatment for patients under 19.

Researchers here take a very broad tour of the established literature on the comparative biology of aging in long lived species of all sorts, picking from those that can live more than 250 years, whether plant or animal, and comparing reported differences in biochemistry both between species and between individuals of the same species. It seems just as interesting to ask which mechanisms are important in individual variation in pace of aging in a long-lived species as to ask why the species is long-lived in the first place. The usual challenges exist, in that one can identify differences in biochemistry that seem reasonably likely to contribute to differences in longevity, but establishing the relative importance of each contribution is near impossible without some form of […]

OpenEvidence, an AI tool used by American doctors, is now being offered in countries with limited access to medical literature. Reuters reported that the company is working with Anthropic to give clinicians in low- and middle-income countries free access to a specialized version of its platform. The initiative is being introduced in around 100 countries, […] This story continues at The Next Web

New York University researchers have trained an AI model to learn chemical patterns associated with stability in drug-like molecules and accurately predict where their hydrogen atoms should be positioned.

Large language models are being welcomed into hospitals at a pace that has outstripped nearly every safety discipline in modern medicine. They draft discharge summaries, suggest differential diagnoses, and increasingly sit beside clinicians during time-critical decisions. Yet the yardstick most commonly used to judge them—aggregate accuracy on standardized benchmarks—may be quietly concealing the very failures […]

AI video platform Synthesia is among the companies shipping tools that translate video into other languages using AI.

arXiv:2609.25043v1 Announce Type: cross Abstract: Quantum encrypted cloning encodes an unknown state into several encrypted components, each offering an alternative way to recover it later. We show that this redundancy can also serve for one-shot fault diagnosis: instead of inspecting the encrypted state, we measure relational Pauli observables testing consistency conditions imposed by the encoding. The canonical Yamaguchi--Kempf scheme encodes the input into \(n\) signal--key pairs, all carrying the same coherent Bell label, plus a transformed copy of the input qubit. Comparing the labels of two pairs yields a deterministic check that localizes an anomalous pair and identifies its Pauli-error class without revealing the label. Such checks cannot tell whether the signal or the key of that pair is faulty, and no measurement on the pairs can (we prove that they already generate the whole group of deterministic state-blind observables supported there, of rank \(2(n-1)\)). This ambiguity

arXiv:2609.26072v1 Announce Type: new Abstract: Inter-agent communication is essential to multi-agent language-model systems, yet a single message may combine task-critical information with instructions not authorized by the original request. Prompt-based defenses leave enforcement to models exposed to adversarial messages, while indiscriminate message removal discards useful information. We introduce Executable Semantic Commitments with Clean-Room Recovery (ESC-CR), a policy-backed framework for secure inter-agent code generation and recovery. It separates message claims from authorization, constructs executable commitments from trusted tasks, evidence, and policy, and enforces them at an external release boundary. Upon a violation, ESC-CR taints the responsible message and rejected artifact, reconstructs a clean context from evidence-backed task information, and regenerates under the same policy. We evaluate ESC-CR across communication-essential and standard code-generation

arXiv:2609.25756v1 Announce Type: new Abstract: Precision medical robotics demands adaptive decision-making under strict safety, interpretability, and execution constraints. Although recent Vision-Language-Action (VLA) models show strong multimodal reasoning ability, their continuous action generation paradigm is not well suited for precision medical tasks, where reliable closed-loop operation may also depend on non-action system function calls. To address this gap, we propose MedVLA, a hierarchical framework that couples high-level multimodal reasoning with low-level function-constrained execution. We further introduce a scalable multi-agent pipeline to generate skill-oriented chain-of-thought(CoT) data for structured training. Built on different multimodal large-model backbones, MedVLA consistently improves performance after fine-tuning, demonstrating the effectiveness of the proposed framework across model variants. Under identical initial conditions, we perform 100 closed-loop

arXiv:2609.25642v1 Announce Type: new Abstract: Closed-loop evaluation of surgical robots requires tissue that deforms, can be grasped and lifted, and reproduces the anatomy in which the robot will operate. We present a simulator in which this tissue is reconstructed from a fixed-view RGB-D recording of the surgical field, composited to remove the instruments, closed into watertight volumes and tetrahedralised; the pipeline was applied unchanged to three specimens of two species (thirteen organs, 146,061 tetrahedra, no inverted elements). For one specimen, the organs are placed in a bimanual cell in which two Franka FR3 arms operate motorised instruments through 6 mm trocars. The core contribution is the numerical and contact design that keeps this cell stable: implicit integration, simulation meshes separate from collision meshes, numerical guards, and a grasp constraint captured at the live tissue pose. In 45 repeated grasp-lifts, a friction grasp held the tissue in 0 of 15 trials

Crohn’s disease is one of the most stubborn forms of inflammatory bowel disease, marked by chronic inflammation of the right colon and terminal ileum that brings diarrhea, abdominal pain, and sometimes life-threatening intestinal obstruction. Roughly twelve percent of patients carry a genetic predisposition, with certain populations showing heightened risk, and although corticosteroids, thiopurines, biologics, and […]

Sunlight leaves its signature on skin over decades: thickened, leathery patches, deepening wrinkles, broken capillaries, and uneven pigment that dermatologists collectively call photoaging. Beyond its cosmetic toll, chronic ultraviolet exposure can progress to precancerous actinic keratosis and even cutaneous malignancies, making it a genuine medical problem rather than a purely aesthetic one. Current remedies all […]

Bone marrow mesenchymal stem cells, or BMSCs, are the quiet workhorses of the skeleton. They replenish bone-forming osteoblasts throughout life, and their regenerative power underlies an expanding range of experimental therapies, from grafting cells into fracture sites to engineering scaffolds that coax new bone to grow. Yet these cells have a persistent enemy: oxidative stress. […]

High on the dry, sun-scorched slopes of the northwestern Himalayas grows one of the region’s most valuable and most vulnerable trees: Pinus gerardiana, the Chilgoza pine. Prized for its edible seeds, which fetch premium prices in local and international markets, and revered in traditional medicine, this endemic conifer is now classified as near-threatened on the […]

A team of researchers in China has developed a machine learning tool that can predict, before a single incision is made, whether a woman’s breast cancer has begun its silent spread through lymphatic and blood vessels. The finding, published in Cancer Reports, could change how surgeons plan operations and how oncologists tailor drug therapy, because […]

Cardiovascular disease remains the world’s deadliest health problem, claiming 19.2 million lives in 2023, with prevalent cases climbing to a record 626 million. Yet the tools scientists use to study the heart and test new drugs have lagged far behind this growing burden. A major new review published in Bioengineering & Translational Medicine argues that […]

Deep beneath the surface of coastal waters, colonies of a small marine invertebrate called Hydractinia symbiolongicarpus perform feats of regeneration that would make any mammalian tissue envious. These colonial cnidarians, related to jellyfish and corals, can regrow lost body parts throughout their lives, thanks to a population of adult stem cells known as interstitial cells, […]

Researchers combined Raman microscopy with gene expression data at single-cell resolution from the same cells, and AI, to develop RamanOmics, a noninvasive way to detect biomarkers of cellular senescence as “barcodes." The post Cell Senescence ‘Barcodes’ Identified with Raman Microscopy and Gene Expression Data appeared first on GEN - Genetic Engineering and Biotechnology News.

A rare and devastating inherited immune disorder may have a new path toward treatment, thanks to a proof-of-concept study demonstrating that CRISPR base editors can correct disease-causing mutations in the Artemis gene outside the body. Artemis-deficient severe combined immunodeficiency, known as ART-SCID, leaves infants with almost no functional T and B cells, and current treatments […]

Deep in the pharmacopoeia of Tibetan medicine lies a vast library of plants whose correct identification can mean the difference between a healing remedy and a useless or even harmful preparation. For centuries, that identification has depended on the trained eyes of practitioners, but a research team in Qinghai, China, now reports a machine learning […]

Cirrhosis can recur after liver transplantation, according to a study published online Sept. 3 in Portal Hypertension & Cirrhosis.

Most medical devices do not enter the market through rigorous safety testing but by being deemed similar enough to something already approved—the "predicate" device—through a mechanism known as the FDA's 510(k) pathway. But similar is not a synonym for safe. While the assumption may be that substantial equivalence is a reasonable stand-in for a safety review, some devices cleared with this method are still recalled, and the FDA spends valuable time reviewing devices the same way, regardless of how risky they appear on paper.

Sony's filings describe AI-generated diagnostic code for connected devices, while one application faced a final rejection before publication

Lithium-ion batteries quietly age every time they charge and discharge, and knowing exactly how much life remains inside a cell has become one of the most consequential measurement problems in modern energy technology. Electric vehicles, grid-scale storage systems and consumer electronics all depend on accurate estimates of the state of health, the measure that links […]

Inside every bacterial cell, RNA molecules carry far more information than their sequence of bases alone. After transcription, the four nitrogenous bases of RNA can be chemically altered by specialized enzymes, and these modifications influence how stable the molecules are, how efficiently they are translated into protein, and how the cell copes with stress. The […]

Every year, the world applies millions of tonnes of agrochemicals to crops and consumes billions of doses of pharmaceuticals, yet the safety story rarely ends when these compounds do their intended job. Once released into soil, water, and the human body, pesticides, herbicides, fungicides, and drugs are transformed by sunlight, microbes, plants, and metabolism into […]

The global spread of highly pathogenic avian influenza has exposed a persistent weakness in the world’s diagnostic arsenal: the tools that are most sensitive tend to be locked inside well-equipped laboratories, while the faster, simpler tests sacrifice the specificity needed to track emerging viral lineages. A research team led by Yujia Huang and Andrew Guo […]

Glioblastoma remains the most feared diagnosis in neuro-oncology. Despite surgery, radiotherapy, and chemotherapy, the tumor almost invariably returns, driven in part by its extraordinary cellular diversity and by a microenvironment that actively shelters malignant cells from treatment. Gene therapy delivered directly into the resection cavity offers one possible route forward, and adeno-associated virus (AAV) vectors […]

Treatment resistance remains one of the most stubborn obstacles in modern oncology, and a comprehensive new review published in the journal Molecular Cancer argues that a humble laboratory tool — the patient-derived organoid — may finally offer researchers a way to see the full architecture of that resistance in a single, living system. Writing as […]

Drug-induced seizures remain one of the most disruptive safety failures in modern pharmaceutical research, derailing promising molecules across therapy areas as diverse as the central nervous system, cardiovascular medicine, gastroenterology, respiratory disease and inflammation. Traditionally, seizurogenic risk only surfaces late, during rodent and non-rodent toxicology studies or, worse, once a compound has already entered clinical […]

State laws to combat disability-based discrimination in the organ transplant process aren't working, according to new research from The Ohio State University College of Medicine. The study, published in JAMA Internal Medicine, examines national policies designed to help all patients have a fair chance to receive an organ transplant. Despite 40 states passing laws prohibiting disability-based discrimination in the organ transplant process, people with intellectual and/or developmental disabilities (IDD) are still less likely to receive a kidney transplant than those without IDD.

4D microscopy gives AI a moving picture of the cell. Continue reading AI-built “Virtual Cells” could speed up drug discovery on Tech Explorist.

A sweeping new review argues that CRISPR-based gene editing could become one of the most consequential tools ever applied to African agriculture, but only if the continent can close persistent gaps in laboratory infrastructure, regulation, funding and seed delivery. The analysis, published in the journal Discover Agriculture, synthesizes nearly a decade of evidence on gene […]

Research from stem cell charity Anthony Nolan, published in Transplantation and Cellular Therapy, has revealed that 1 in 50 people studied has an "especially useful" gene variant that could make them a particularly desirable stem cell donor.

Nigerian surgeons remotely removed a cancer-affected kidney in West Africa’s first tele-robotic surgery Read Full Article at RT.com

When a failing heart is replaced through transplantation, or its workload is offloaded by a mechanical pump, physicians expect the body’s stress chemistry to calm down. The rationale seems straightforward: heart failure is driven in large part by a runaway neurohormonal response, and if the hemodynamic catastrophe is corrected, that response should switch off. A […]

Few technologies have unsettled the conventions of pharmaceutical research quite like induced pluripotent stem cells, or iPSCs. A sweeping review published in Discover Biotechnology examines how, between 2020 and 2024, these reprogrammed human cells have moved from laboratory curiosity to a central engine of novel drug development, offering researchers something that has long been out […]

A new government program that will push the boundaries of AI in medicine could transform how the US cares for patients with heart failure and eventually other chronic diseases. But that’s only if the public’s ...

Senescent cells accumulate with age, likely largely because the aging of the immune system slows down the clearance of senescent cells, but the relative importance of different contributions to the growing burden of senescence in aging tissues is an area of ongoing discussion. Senescent cells secrete inflammatory signals that are disruptive to tissue structure and function when sustained over the long term. Separately, cells throughout the body accumulate mutations over the course of aging. Much of this has little to no effect, occurring in cells with few replications remaining, or in genes not used by the cell. However, a growing burden of mutation in stem cell populations spreads slowly into the tissues they support via the daughter somatic cells generated to replace those cells lost […]

arXiv:2609.24842v1 Announce Type: cross Abstract: Proteins can possess numerous mutations relative to their wild-type amino acid sequences with minimal impact to their structure and function. However, in other cases, even a single amino acid mutation relative to the wild-type sequence can lead to a large change in structure or even a disease phenotype. While the accuracy of wild-type protein structure prediction has improved significantly in recent years, it remains difficult to accurately predict the structure of mutant proteins. Here, we characterize the local mutation-induced structural changes in proteins for a dataset of wildtype and the corresponding single-amino acid mutant x-ray crystal structures from the Protein Data Bank (PDB). We find that mutation-induced structural changes in these proteins are localized at the site of the mutation, decaying rapidly with increasing spatial distance from the mutation site. In addition, we evaluate how well AlphaFold3 can recapitulate the

arXiv:2609.24842v1 Announce Type: new Abstract: Proteins can possess numerous mutations relative to their wild-type amino acid sequences with minimal impact to their structure and function. However, in other cases, even a single amino acid mutation relative to the wild-type sequence can lead to a large change in structure or even a disease phenotype. While the accuracy of wild-type protein structure prediction has improved significantly in recent years, it remains difficult to accurately predict the structure of mutant proteins. Here, we characterize the local mutation-induced structural changes in proteins for a dataset of wildtype and the corresponding single-amino acid mutant x-ray crystal structures from the Protein Data Bank (PDB). We find that mutation-induced structural changes in these proteins are localized at the site of the mutation, decaying rapidly with increasing spatial distance from the mutation site. In addition, we evaluate how well AlphaFold3 can recapitulate the

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Stem cell transplants helped regenerate stroke-damaged brain tissue in mice, producing new neurons and restoring lost motor function. The treatment also improved blood vessels, inflammation, and the blood-brain barrier, raising hopes that a similar approach could eventually help repair the human brain after stroke.

A noncontiguous code for RNA-guided DNA recognition at the origin of CRISPR-Cas  Science | AAASDiscovery of CRISPR's long lost ancestor may expand gene-editing toolkit  Phys.orgThe Next Gene-Editing Technology May Also Be the Oldest  The New York Times

A noncontiguous code for RNA-guided DNA recognition at the origin of CRISPR-Cas  Science | AAASDiscovery of CRISPR's long lost ancestor may expand gene-editing toolkit  Phys.orgThe Next Gene-Editing Technology May Also Be the Oldest  The New York Times

Ученые ЦНИИ Эпидемиологии Роспотребнадзора разработали тест-систему, которая позволяет выявлять ген устойчивости бактерий к метициллину. Новинку создали на основе технологии CRISPR/Cas.

Marine scientists have been amazed to discover an endangered sea cucumber can live for decades, with some animals living more than 100 years, in a first-of-its-kind genetic mark-recapture study. Australian Institute of Marine Science (AIMS) Senior Principal Research Scientist Dr. Sven Uthicke said the findings suggested black teatfish sea cucumber populations recover much more slowly than previously thought and that this had implications for commercial fishery catch limits.

Artificial intelligence is rapidly transforming how one of medicine’s most information-rich cancer scans is read, and a new comprehensive review argues that lymphoma may be the field where the change hits hardest. Published in Holistic Integrative Oncology, the review systematically synthesized 53 original studies, selected from an initial pool of more than 1,000 papers under […]

For more than a decade, cellular senescence has been one of the most compelling stories in aging research. Senescent cells—viable but permanently arrested cells that secrete inflammatory molecules—accumulate in tissues over time, and landmark animal studies showed that chemically clearing them can extend lifespan and ease a remarkable range of age-related diseases. Now, a comprehensive […]

Artificial intelligence is transforming medicine at breathtaking speed, diagnosing heart disease from electrocardiograms, flagging sepsis hours before clinicians suspect it, and drafting clinical notes in seconds. Yet a new commentary in the Journal of Medical Systems argues that the hardest problems facing clinical AI are not computational at all. They are philosophical. Antonis A. Armoundas […]

Researchers identified genes that enable the regeneration of dopamine-producing neurons in planarians. This provides a roadmap for investigating whether similar pathways can be activated in humans and potentially leveraged to treat traumatic brain injuries and neurodegenerative diseases. The post Genes Involved in Flatworm Brain Regeneration Identified appeared first on GEN - Genetic Engineering and Biotechnology News.

Beacon Therapeutics said on Monday its experimental gene therapy improved the ability to read ⁠in low-light conditions in a late-stage trial on people with a form of...

RamanOmics decodes the spatial vibrational–molecular architecture of senescence in aging and repair  NatureUnmasking “zombie cells” in aging tissue with an AI-powered barcode  MIT NewsHarvard Medical School uses RamanOmics to barcode senescent ‘zombie cells’ and measure biological age  dongascience.comThe chemical fingerprint of cellular senescence  Nature

RamanOmics decodes the spatial vibrational–molecular architecture of senescence in aging and repair  NatureUnmasking “zombie cells” in aging tissue with an AI-powered barcode  MIT NewsHarvard Medical School uses RamanOmics to barcode senescent ‘zombie cells’ and measure biological age  dongascience.comThe chemical fingerprint of cellular senescence  Nature

Radicals, atoms or molecules that readily react with other substances to form new bonds, are useful tools for building complex substances such as pharmaceuticals. But even when a radical is generated efficiently, the reaction cannot continue unless the catalyst returns to its original state.

Companies have invested heavily in workplace mental health, yet many employees and managers are still struggling. The next evolution is helping people build the capacity to perform, adapt and grow as the demands of work continue to change.

Researchers led by Assistant Professor Lynn Yap of the Lee Kong Chian School of Medicine at Nanyang Technological University, Singapore, have uncovered new insights into how unspecialized cells, also known as stem cells, develop and mature into heart muscle cells. The findings could pave the way for new treatments for heart disease.

Sanfilippo syndrome type A (MPS IIIA) is a rare, fatal lysosomal storage disease that primarily affects the central nervous system and is marked by rapid neurodegeneration beginning in early childhood. The post Andelyn Curator Biomanufacturing Platform Supports Fayuvi Gene Therapy Approval appeared first on GEN - Genetic Engineering and Biotechnology News.

Bone marrow transplants offer an unexpected way for diseased cells in the heart and brain to get replacement parts, a Stanford Medicine-led study has shown. The finding offers hope for the first effective treatment of mitochondrial disorders, a group of genetic diseases in which cells' motors, called mitochondria, are dysfunctional.

The collaboration combines Biographica’s computational platform for identifying high-value gene targets and Hudson River’s expertise in gene-editing. The post ‘Bring us your difficult trait problems’: Biographica, Hudson River partner on crop genome editing appeared first on AgFunderNews.

Brock E.W. Turner / Axios: NYC-based Corridor, which uses AI to offer health benefits for small businesses, raised a $16M seed led by Bain Capital Ventures, following a $9M pre-seed  —  Corridor, an AI-native health benefits broker, raised $16 million in seed funding led by Bain Capital Ventures, CEO Nikhil Aggarwal tells Axios Pro exclusively.